The Hidden Burden: Gastrointestinal Involvement in Lysosomal Storage Disorders by Vincenza Gragnaniello, Chiara Cazzorla, Daniela Gueraldi, Andrea Puma, Christian Loro, Alberto B. Burlina

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Transitioning into Adulthood with PKU: The Role of Diet, Coping Strategies, and Quality of Life in Adolescents and Young Adults by Chiara Cazzorla, Giacomo Gaiga, Silvia Medici, Ludovica Martino, Vincenza Gragnaniello, Rossana Schiavo, Alessandro P. Burlina, Alberto B. Burlina

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Case Report: Novel treatment approach for severe interstitial lung disease in type 3 Gaucher disease by Vincenza Gragnaniello, Vincenza Gragnaniello, Silvia Carraro, Tiziana Zangardi, Chiara Cazzorla, Daniela Gueraldi, Alberto B. Burlina, Alberto B. Burlina

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Newborn Screening for Gaucher Disease: Parental Stress and Psychological Burden by Chiara Cazzorla, Vincenza Gragnaniello, Giacomo Gaiga, Daniela Gueraldi, Andrea Puma, Christian Loro, Giada Benetti, Rossana Schiavo, Elena Porcù, Alessandro P. Burlina, Alberto B. Burlina

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