Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency - Samia L. Pratt; Mariana Zarate-Mendez; Lidiia Koludarova; Sonja Jansson; Mikko Airavaara; Irena Hlushchuk; David Coleman; Caleb Heffner; Rita Horvath; Brendan J. Battersby; Robert W. Burgess (Disease Models & Mechanisms)